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Sodium phenylacetate
Hyperammonaemia in urea cycle disorders and in undiagnosed patient with hyperammonaemia, no evidence support its use in acute crises of propionic or methylmalonic acidemia.
IV or PO
Endocrine metabolic: Hyperammonemia (5%), Hypokalemia (7%), Metabolic acidosis (4%).
Hematologic: Anemia (4%), Disseminated intravascular coagulation (3%).
Neurologic: Cerebral edema (5%), Coma (3%), Neurotoxicity, Seizure (6%).
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22. Kranen S, Keough D, Gordon RB, Emmerson BT. Xanthine-containing calculi during allopurinol therapy. J Urol 1985;133(4):658-9
104. Wraith JE, Clarke LA, Beck M, et al. Enzyme replacement therapy for mucopolysaccharidosis I: a randomized, double-blinded, placebo-controlled, multinational study of recombinant human alpha-L-iduronidase (laronidase). J Pediatr 2004;144(5):581-8 doi: 10.1016/j.jpeds.2004.01.046[published Online First: Epub Date]|.